miglustat
Selected indexed studies
- Miglustat. (, 2012) [PMID:31643565]
- Miglustat. (, 2006) [PMID:32352698]
- Miglustat. (Drugs, 2003) [PMID:14609352]
_Worker-drafted node — pending editorial review._
Connections
No connections recorded yet.
Sources
- Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease (PROPEL): an international, randomised, double-blind, parallel-group, phase 3 trial. (2021) pubmed
- 104-week efficacy and safety of cipaglucosidase alfa plus miglustat in adults with late-onset Pompe disease: a phase III open-label extension study (ATB200-07). (2024) pubmed
- Miglustat. (2003) pubmed
- Miglustat. (2012) pubmed
- Miglustat. (2006) pubmed
- Miglustat (Zavesca®). (1994) pubmed
- Miglustat (Zavesca®). (1994) pubmed
- Miglustat in Niemann-Pick disease type C patients: a review. (2018) pubmed
- Miglustat: a first-in-class enzyme stabilizer for cipaglucosidase alfa for the treatment of late-onset Pompe disease. (2026) pubmed
- Efficacy and safety of miglustat in the treatment of GM2 gangliosidosis: A systematic review. (2023) pubmed