betibeglogene autotemcel Zynteglo
Selected indexed studies
- Betibeglogene Autotemcel Gene Therapy for Non-β(0)/β(0) Genotype β-Thalassemia. (N Engl J Med, 2022) [PMID:34891223]
- Betibeglogene autotemcel (Zynteglo) for beta thalassemia. (Med Lett Drugs Ther, 2024) [PMID:39302350]
- Betibeglogene autotemcel gene therapy in patients with transfusion-dependent, severe genotype β-thalassaemia (HGB-212): a non-randomised, multicentre, single-arm, open-label, single-dose, phase 3 trial. (Lancet, 2024) [PMID:39527960]
_Worker-drafted node — pending editorial review._
Connections
No connections recorded yet.
Sources
- Betibeglogene Autotemcel Gene Therapy for Non-β(0)/β(0) Genotype β-Thalassemia. (2022) pubmed
- Gene therapy in transfusion-dependent non-β0/β0 genotype β-thalassemia: first real-world experience of beti-cel. (2025) pubmed
- Betibeglogene autotemcel gene therapy in patients with transfusion-dependent, severe genotype β-thalassaemia (HGB-212): a non-randomised, multicentre, single-arm, open-label, single-dose, phase 3 trial. (2024) pubmed
- Clinical applications of gene therapy for rare diseases: A review. (2023) pubmed
- Betibeglogene autotemcel (Zynteglo) for beta thalassemia. (2024) pubmed
- Long-term efficacy and safety results of betibeglogene autotemcel gene therapy for transfusion-dependent β-thalassemia. (2026) pubmed
- Zynteglo: Betibeglogene autotemcel - An innovative therapy for β- thalassemia patients. (2022) pubmed
- Betibeglogene Autotemcel; A New Hope For Transfusion Dependent Beta-Thalassaemia. (2023) pubmed
- Cell-Based Gene Therapy for b-Thalassemia. (2023) pubmed
- Drug product attributes predict clinical efficacy in betibeglogene autotemcel gene therapy for β-thalassemia. (2023) pubmed