base editing therapeutic
Selected indexed studies
- Base editing: advances and therapeutic opportunities. (Nat Rev Drug Discov, 2020) [PMID:33077937]
- CRISPR-Cas9 DNA Base-Editing and Prime-Editing. (Int J Mol Sci, 2020) [PMID:32872311]
- Therapeutic base editing of human hematopoietic stem cells. (Nat Med, 2020) [PMID:32284612]
_Worker-drafted node — pending editorial review._
Connections
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Sources
- Base editing: advances and therapeutic opportunities. (2020) pubmed
- CRISPR-Cas9 DNA Base-Editing and Prime-Editing. (2020) pubmed
- Therapeutic base editing of human hematopoietic stem cells. (2020) pubmed
- Base editing: precision chemistry on the genome and transcriptome of living cells. (2018) pubmed
- Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease. (2025) pubmed
- Recent advances in therapeutic gene-editing technologies. (2025) pubmed
- Base editing of haematopoietic stem cells rescues sickle cell disease in mice. (2021) pubmed
- Mitochondrial Base Editing: Recent Advances towards Therapeutic Opportunities. (2023) pubmed
- Base Editing and Prime Editing: Potential Therapeutic Options for Rare and Common Diseases. (2023) pubmed
- Gene and Base Editing as a Therapeutic Option for Cystic Fibrosis-Learning from Other Diseases. (2019) pubmed